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Rare Disease Stakeholders: Do mRNA COV19 Vaccines Affect Eligibility to Receive Future Gene Therapy?
The American Society of Gene and Cell Therapy issued FAQs on December 30, 2020 to explain how mRNA vaccines for COVID19 work and why they...
The Impact of Single Indication Orphan Drugs on the Future of Rare Diseases
What is the impact of rare diseases on individuals and health care systems?
Congressionally funded report details diagnostic challenges and costs of rare diseases in the US
Diagnostics: Moving to the forefront of Global Healthcare
Economic Burden of Rare Diseases Nearly $1 Trillion
CBO Comparison of Brand-Name Drug Prices Among Selected Federal Programs
Orphan drugs account for more than half of all FDA drug approvals in 2020
Rare Disease Stakeholders: Do mRNA COV19 Vaccines Affect Eligibility to Receive Future Gene Therapy?
How do we identify and measure value for patients with rare diseases?
National Burden of Rare Disease Survey
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