August - 2020

How do we identify and measure value for patients with rare diseases?

Rare diseases impact 1 in 10 Americans, and over 400 million people worldwide. The current development and FDA approval process can cost hundreds of millions of dollars – and take an average of 15 years – to develop one therapy. For the 30% of children diagnosed with a rare disease, who won’t live to see their 5th birthday, this wait is unthinkable. Meanwhile, prolonged – and unnecessary – diagnostic delays and inadequate treatment protocols yield increased healthcare costs a

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Economic Burden of Rare Diseases Nearly $1 Trillion

CBO Comparison of Brand-Name Drug Prices Among Selected Federal Programs

Orphan drugs account for more than half of all FDA drug approvals in 2020

Rare Disease Stakeholders: Do mRNA COV19 Vaccines Affect Eligibility to Receive Future Gene Therapy?

How do we identify and measure value for patients with rare diseases?

National Burden of Rare Disease Survey

HVH Precision Analytics and Diligentia Strategy Announce Upcoming Presentation at the 2020 American

Planning for a New Era: Commercial Strategy under the Lens of Public Scrutiny

Meet with us at the 38th annual J.P. Morgan Healthcare Conference, January 13-16, 2020

Meet with us at the RARE Patient Advocacy Summit, September 18-20, 2019

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